Miglustat for treatment of Niemann-Pick C disease: a randomised

Dermatologic Manifestations of Niemann-Pick Disease: Background, Pathophysiology, Etiology

Diagnostic workup and management of patients with suspected Niemann-Pick type C disease - Apostolos Papandreou, Paul Gissen, 2016

Niemann-Pick type C disease: molecular mechanisms and potential therapeutic approaches. - Abstract - Europe PMC

Miglustat, C10H21NO4

Subcortical Volumetric Reductions in Adult Niemann-Pick Disease Type C: A Cross-Sectional Study

Niemann-Pick Disease, Type a disease: Malacards - Research Articles, Drugs, Genes, Clinical Trials

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Investigation of 2-Hydroxypropyl-β-Cyclodextrin Treatment in a Neuronal-Like Cell Model of Niemann–Pick Type C Using Quantitative Proteomics

5 Most Promising Companies offering hope to patients with Niemann-Pick Type C

Patient with Niemann-Pick disease type C: over 20 years' follow-up

Recommendations for the diagnosis and management of Niemann–Pick disease type C: An update - ScienceDirect

PDF] Miglustat for treatment of Niemann-Pick C disease: a randomised controlled study

Recent advances in the treatment of Niemann pick disease type C: A mini-review - ScienceDirect

Unbiased yeast screens identify cellular pathways affected in Niemann–Pick disease type C

PDF] Miglustat for treatment of Niemann-Pick C disease: a randomised controlled study