Strategies to combat Tay-Sachs disease - ScienceDirect

Long-Term Correction of Sandhoff Disease Following Intravenous Delivery of rAAV9 to Mouse Neonates: Molecular Therapy

PDF] Tay-Sachs Disease: Mechanisms of Neuropathology and Potential Therapeutic Strategies Utilizing Human Lysosomal Sialidase

Spontaneous appearance of Tay–Sachs disease in an animal model - ScienceDirect

Natural history of Tay-Sachs disease in sheep - ScienceDirect

Spontaneous appearance of Tay–Sachs disease in an animal model - ScienceDirect

Frontiers New Approaches to Tay-Sachs Disease Therapy

Targeting the central nervous system in lysosomal storage diseases: Strategies to deliver therapeutics across the blood-brain barrier - ScienceDirect

Neurological manifestations of lysosomal disorders and emerging therapies targeting the CNS - The Lancet Child & Adolescent Health

Spontaneous appearance of Tay–Sachs disease in an animal model - ScienceDirect

Introduction of an N-Glycan Sequon Into HEXA Enhances Human β-Hexosaminidase Cellular Uptake in a Model of Sandhoff Disease: Molecular Therapy