Searching for a cure for Niemann-Pick Type C - NemaMetrix

Niemann-Pick Type C is a rare and fatal disorder affecting children. We explore the efficacy of new potential therapeutics with the ScreenChip System.

Health Tip on New Treatment that Shows Promise in Niemann-Pick Type C Disorder - Health Tips

WEBINAR “Niemann-Pick Type C: Two Genes - Many Clinical Pictures - One Unifying Biomarker”

Recent advances in the treatment of Niemann pick disease type C: A mini-review - ScienceDirect

PDF) Long-Term Treatment of Niemann-Pick Type C1 Disease With Intrathecal 2-Hydroxypropyl-Β-Cyclodextrin

Searching for a cure for Niemann-Pick Type C - NemaMetrix

5 Most Promising Companies offering hope to patients with Niemann-Pick Type C

Searching for a cure for Niemann-Pick Type C - NemaMetrix

White and gray matter alterations in adults with Niemann-Pick disease type C

Searching for a cure for Niemann-Pick Type C - NemaMetrix

Elucidating the mechanism of cyclodextrins in the treatment of Niemann-Pick Disease Type C using crosslinked 2-hydroxypropyl-β-cyclodextrin

IJMS, Free Full-Text

PDF) Long-Term Treatment of Niemann-Pick Type C1 Disease With Intrathecal 2-Hydroxypropyl-Β-Cyclodextrin

Treatment Options for Niemann-Pick Type C

Niemann–Pick type C disease as proof‐of‐concept for intelligent biomarker panel selection in neurometabolic disorders - Papandreou - 2022 - Developmental Medicine & Child Neurology - Wiley Online Library