Niemann-Pick disease Information

Learn about Niemann-Pick disease, find a doctor, complications, outcomes, recovery and follow-up care for Niemann-Pick disease.
Learn more about Niemann-Pick disease, diagnosis, causes, symptoms, and treatment options at Mount Sinai Health System.

Understanding the phenotypic variability in Niemann-Pick disease type C (NPC): a need for precision medicine

Niemann-Pick disease Information

Niemann-Pick Type C « Niemann-Pick Children's Fund, Inc

Niemann- Pick Disease Type C (NPC) Market Report 2023-2033 - Wissen Research

Science Update: Biomarker for Niemann-Pick type C may be useful for diagnosing other class of rare disorders, NIH study suggests

Treatment outcomes following continuous miglustat therapy in patients with Niemann-Pick disease Type C: a final report of the NPC Registry, Orphanet Journal of Rare Diseases

Parents of kids with Niemann Pick C advocate for adrabetadex

Niemann–Pick disease - Wikipedia

Bone marrow involvement in Niemann Pick disease - 1.

Niemann Pick Disease - an overview