Niemann-Pick Type C « Niemann-Pick Children's Fund, Inc

What is Niemann-Pick Type C Disease (NPC)? Niemann-Pick Type C Disease (NPC) simply put is FATAL. It is a genetic, neurodegenerative disorder that consequently accumulates large amounts of choleste…

Clinical disease characteristics of patients with Niemann-Pick

In the news: Brave Mum of 3 children with Niemann-Pick disease type C

Miglustat for treatment of Niemann-Pick C disease: a randomised

Niemann-Pick disease

Genetic disease and Niemann-Pick disorders: novel treatments and

Niemann-Pick disease type C symptomatology: an expert-based

Intrathecal 2-hydroxypropyl-β-cyclodextrin decreases neurological

The National Niemann-Pick Type C1 Disease Database: correlation of

Cyclo Therapeutics, Inc. - All forms of Niemann-Pick disease (#NPD

What is Niemann-Pick Type C Disease?

What is Niemann-Pick Type C Disease?

Jill Beirl – NNPDF